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Derniers dépôts
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Nombre de documents
791
Nombre de notices
1 380
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AAV
Myotonic Dystrophy
CMS
Fabry disease
Heart
Autophagy
Satellite cells
Gene therapy
Laminopathy
Biomarker
Mouse model
Mechanotransduction
Motoneuron
Myopathy
Dermatomyositis
Autoimmune diseases
Myotonic dystrophy
Laminopathies
Dystrophin
Transcriptomics
Rare diseases
Dilated cardiomyopathy
Myopathies
MBNL
Myotonic Dystrophy type 1
Neuromuscular disease
Satellite cell
CTG repeat contractions
Dynamin 2
Clinical trials
Thymus
Myasthenia Gravis MG
Transgenic mouse model
Muscle regeneration
Biomarkers
Regeneration
Long read sequencing
ALS
Amyotrophic lateral sclerosis
Male
Lamin A/C
Rare neuromuscular diseases
Myasthenia gravis
Exercise
LMNA gene
Autoantibodies
Actin
Neuromuscular junction
LMNA
Alternative splicing
Cytoskeleton
Laminopathie
Myositis
Animals
Aging
Nuclear envelope
PABPN1
Treatment
Errance diagnostique
Mice
Heart failure
Inflammation
Astrocyte
Centronuclear myopathy
Calcium
Outcome measures
Glutamate
RNA interference
Cardiomyopathy
Cancer
Cell therapy
Therapy
Lamin A/C LMNA gene
Skeletal muscle
Genotype phenotype correlation
OPMD
Muscular dystrophy
Myotonic dystrophy type 1
DMD
Antisense oligonucleotides
Muscle
Humans
Brain
Myogenesis
Duchenne muscular dystrophy
Myoblasts
Aged
Becker muscular dystrophy
Fibrosis
Cytokines
Congenital myopathy
Congenital muscular dystrophy
Thérapie génique
CRISPRi
Autoimmunity
Neuromuscular diseases
Trinucleotide repeat expansion
RNA biology
COVID-19
FSHD
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